Dubai Becomes First City Outside the US to Administer Groundbreaking Gene Therapy for Adult SMA Patient
Dubai achieves global first with breakthrough gene therapy for adult SMA patient
Gulf News
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Dubai has achieved a significant medical milestone by administering a newly licensed gene therapy to a 22-year-old Egyptian patient with Spinal Muscular Atrophy (SMA). This marks the first instance outside the United States where an adult has received this treatment, expanding access for older patients who previously had limited options.
- 01Dubai is the first location outside the US to administer gene therapy for adult SMA patients.
- 02The treatment was given to a 22-year-old Egyptian patient at Medcare Royal Specialty Hospital.
- 03This therapy, known as Itvisma, targets the root cause of SMA by delivering a functional SMN1 gene.
- 04The achievement opens new possibilities for adult patients previously excluded from such treatments.
- 05Over 190 SMA patients have been treated with advanced gene therapies in Dubai since 2020.
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Dubai has made a groundbreaking achievement in medical science by successfully administering a newly licensed gene therapy to an adult patient with Spinal Muscular Atrophy (SMA), becoming the first city outside the United States to do so. The treatment was delivered to a 22-year-old Egyptian patient at Medcare Royal Specialty Hospital, marking only the second time globally that an adult has received this advanced therapy. Traditionally, gene therapies for SMA have been limited to infants and children under two, leaving adults with few effective options. This new development signifies a turning point in SMA treatment, potentially transforming outcomes for thousands of patients. The therapy, known as Itvisma, works by delivering a functional copy of the SMN1 gene directly into the cerebrospinal fluid, addressing the root cause of the disease. Medical experts believe that expanding treatment capabilities to adults will rewrite the life stories of many patients, allowing them to access advanced therapies previously unavailable to them. Since 2020, Dubai has treated over 190 SMA patients with advanced gene therapies, reinforcing its reputation as a hub for medical innovation.
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This breakthrough provides hope for adult SMA patients in Dubai and the wider region, offering them access to advanced treatments that were previously unavailable.
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